Sindy Escobar Alvarez, program director for medical research, speaks with three of the country’s top sickle cell disease researchers to yield insights from the strides being made through their cutting-edge research. In this riveting conversation, Daniel Bauer, M.D., Ph.D, hematologist at Boston Children’s Hospital and associate professor at Harvard Medical School; Donald B. Kohn, M.D., of University of California, Los Angeles; and Punam Malik, M.D., Marjorie Johnson Chair of Gene and Cell Therapy at Cincinnati Children’s Hospital, reveal what they have learned through their work in sickle cell disease research, examine the field’s most substantial challenges and discuss why this is a potent moment of opportunity to accelerate curative therapies for sickle cell disease.
Watch “Breakthroughs in Sickle Cell Disease Research: Promising Approaches in Gene Modification” above or on YouTube.